PROTON Study: SOF + PEG- IFNα-2a + RBV for genotypes 1, 2 and 3
Sofosbuvir in combination with peginterferon alfa-2a and ribavirin for non-cirrhotic, treatment-naive patients with genotypes 1, 2, and 3 hepatitis C infection: a randomised, double-blind, phase 2 trial
Lawitz E. Lancet Infect Dis 2013;13:401-8
Anti-HCV
Sofosbuvir
PEG-IFNα 2a
Ribavirin
Sofosbuvir
PEG-IFNα 2a
Ribavirin
Genotype
1
1a
1b
2
3
1
1a
1b
2
3
Treatment history
Naive
Naive
Cirrhosis
No
No
Design
* Randomisation was stratified on IL28 genotype (CC or non-CC) and HCV RNA (< or = 800,000 IU/ml)
** If eRVR (HCV RNA < 15 IU/ml from W4-12) : 12 additional weeks of PEG-IFN + RBV ; if not, or if in placebo groups, 36 additional weeks
Treatment regimens
- SOF in genotype 1 (double-blind); PEG-IFNα-2a : 180 mg SC once weekly
- RBV weight based (bid dosing) : 1000 mg/day if < 75 kg or 1200 mg/day if ≥ 75 kg
Objective
- Superiority of SOF vs placebo, in combination with PEG-IFN + RBV, in genotype 1 : eRVR (HCV RNA < 15 IU/ml from W4 to W12) > 55% in SOF group (vs 15% in placebo group), 95% power with a 2-sided significance level of 5%
- Safety and tolerability
- Efficacy endpoints
- RVR at week 4
- eRVR (W4-12)
- Response at end of treatment
- SVR12
- SVR24
Baseline characteristics and patient disposition
SVR24 (HCV RNA < 15 IU /ml) % (95% CI)
- Virologic failures in Genotype 1
- Virologic rebound or breakthrough
- 3 in SOF 200 (on PEG-IFN + RBV)
- 2 in placebo
- Post-treatment relapse
- 1 in SOF 200
- 1 in SOF 400
- No resistance emergence at failure
- No S282T mutation by population sequencing
- Virologic rebound or breakthrough
- Difference in SVR24 in Genotype 1
- SOF 200 vs placebo : 28%; 95% CI; 9 to 46, p = 0.0017
- SOF 400 vs placebo : 30% ; 95% CI : 11 to 49, p = 0.0006
Treatment-emergent adverse events (until W12 of SOF)
Grade 3-4 laboratory abnormalities (until W12 of SOF)
Discontinuation for adverse events in Genotype 1, N = 8 ; in Genotype 2-3, N = 0
- 6 in the first 12 weeks
- 3 in the placebo group
- 3 in the SOF 400 group
Summary
- In this phase II trial, patients receiving SOF plus PEG-IFN + RBV had adverse events that were similar in both type and severity to those seen in patients receiving placebo plus PEG-IFN + RBV
- No additional or new adverse events attributable to SOF
- Fatigue, rash, fever, and diarrhea were more commonly seen in patients with HCV genotype-1 receiving SOF than in patients receiving placebo
- During the SOF phase of treatment, response in patients with HCV genotype-1 receiving SOF was much the same, irrespective of dose (200 mg or 400 mg)
- During the PEG-IFN + RBV extension phase of dosing, there were 3 breakthrough post SOF in the 200 mg group vs 0 in the 400 mg group
- In genotype 1 naïve patients, SOF 400 mg 12 weeks (+ PEG-IFN + RBV 24-48 weeks) provided a SVR24 rate 30% higher than placebo
- In patients with HCV genotypes 2 and 3, SVR24 was 92%